Studien

Wertigkeit einer Gruppe von Biomarkern in der Differentialdiagnose von Kindern mit einer ersten demyelinisierenden Erkrankung des ZNS. Multicenter

Multiple Sklerose

Connect (109 MS306) Open-Label, Randomized, Multicenter, Multiple-Dose,Active-Controlled, Parallel-Group, Efficacy and Safety Study of BG00012 in Children

Multiple Sklerose

SNT-III-012 - A Phase III Double blind, Randomized, Placebo Controlled Study assessing the Efficacy, Safety and Tolerability of Idebenone in Patients with Duchenne Muscular Dystrophy Receiving Glucocorticoid Steroids

DSC/14/2357/48 - Givinostat Randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of givinostat in ambulant patients with Duchenne Muscular Dystrophy

ATX-MTM-009 INCEPTUS - A Prospective, Non-Interventional Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects Aged 3 Years and Younger

ATX-MTM-002 ASPIRO A Phase 1/2, Randomized, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate the Safety and Preliminary Efficacy of AT132, an AAV8-Delivered Gene

HINE (ISIS 396443-CS11) An Open-Label Extension Study for Patients With Spinal Muscular Atrophy Who Previously Participated in Investigational Studies of ISIS 396443

CAT-1004-304: POLARIS DMD single global Phase 3 trial called POLARIS DMD in Duchenne to evaluate the efficacy and safety of edasalonexent

A Randomized, Active-Controlled, Open-Label, Flexible-Dose Study to Assess the Safety

and Tolerability of Topiramate as Monotherapy Compared With Levetiracetam as

Monotherapy in Pediatric Subjects With New or Recent-Onset Epilepsy

moma – modules on migraine activity

Strukturierte multimodale Frühintervention für Kinder mit Migräne im Alter von 6-11 Jahren

Deutsches FASD KOMPETENZZENTRUM Bayern