Studien
Laufende Studien – Kooperation LMU
Wertigkeit einer Gruppe von Biomarkern in der Differentialdiagnose von Kindern mit einer ersten demyelinisierenden Erkrankung des ZNS. Multicenter
Multiple Sklerose
2012
laufend
neun
Connect (109 MS306) Open-Label, Randomized, Multicenter, Multiple-Dose,Active-Controlled, Parallel-Group, Efficacy and Safety Study of BG00012 in Children
Multiple Sklerose
2016
laufend
3
neu
NCT 2013-002318-11 EudraCT Number: 2013-002318-11
SNT-III-012 - A Phase III Double blind, Randomized, Placebo Controlled Study assessing the Efficacy, Safety and Tolerability of Idebenone in Patients with Duchenne Muscular Dystrophy Receiving Glucocorticoid Steroids
2016
laufend
3n
neu
DMD/EudraCT Nr.: 2016-000602-10
DSC/14/2357/48 - Givinostat Randomised, double blind, placebo controlled, multicentre study to evaluate the efficacy and safety of givinostat in ambulant patients with Duchenne Muscular Dystrophy
2018
laufend
3
neu
DMD/EudraCT Nr.: 2016-000401-36
ATX-MTM-009 INCEPTUS - A Prospective, Non-Interventional Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects Aged 3 Years and Younger
2016
laufend
natural history
neu
MTM/EudraCT Nr.: 2015-003769-27
ATX-MTM-002 ASPIRO A Phase 1/2, Randomized, Open-Label, Ascending-Dose, Delayed-Treatment Concurrent Control Clinical Study to Evaluate the Safety and Preliminary Efficacy of AT132, an AAV8-Delivered Gene
2018
laufend
1–3
neu
MTM/EudraCT Nr.: 2017-000876-27
HINE (ISIS 396443-CS11) An Open-Label Extension Study for Patients With Spinal Muscular Atrophy Who Previously Participated in Investigational Studies of ISIS 396443
2018
laufend
OLE
neu
SMA/EudraCT Nr.: 2015-001870-16
CAT-1004-304: POLARIS DMD single global Phase 3 trial called POLARIS DMD in Duchenne to evaluate the efficacy and safety of edasalonexent
2018
laufend
3
neu
NCT 03703882
A Randomized, Active-Controlled, Open-Label, Flexible-Dose Study to Assess the Safety
and Tolerability of Topiramate as Monotherapy Compared With Levetiracetam as
Monotherapy in Pediatric Subjects With New or Recent-Onset Epilepsy
2018
3
neu
moma – modules on migraine activity
Strukturierte multimodale Frühintervention für Kinder mit Migräne im Alter von 6-11 Jahren
2018
2021
neu
Deutsches FASD KOMPETENZZENTRUM Bayern
2018
2021
Ethikvotum